Cystic Fibrosis and CFTR: from learning to living

Cystic fibrosis a complex disease caused by mutations in the CFTR gene. These mutations influence how patients experience the disease, so understanding the genetics is the key to understanding CF and its treatment. 

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Information on cystic fibrosis-causing mutations

Information about ORKAMBI® phase III clinical trials

Downloadable KALYDECO® resources



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